Baby KJ's bleak future is brighter as CRISPR breakthrough paves the way to treat rare genetic disorders.

“This is the first step towards the use of gene editing therapies to treat a wide variety of rare genetic disorders for which ...

FRIDAY, May 16, 2025 (HealthDay News) — A baby born with a rare and deadly genetic disease is the world's first known patient ...

News broke yesterday that researchers in Philadelphia appear to have successfully treated a 6-month-old baby boy, called KJ, ...

KJ Muldoon was diagnosed with CPS1 deficiency, which causes toxic levels of ammonia in the blood, soon after his premature ...

A nine-month-old baby has become the first person ever to be successfully treated with personalized gene editing therapy.

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

Doctors announced this week that they have treated a newborn baby with a rare genetic disease using the world’s first personalized gene editing therapy. Geoff Bennett discussed the treatment and its ...

A US infant with a rare condition has become history's first patient to be treated with a personalized gene-editing technique ...

The FDA recently approved a gene-editing technology used to make swine resistant to porcine reproductive and respiratory ...

After hours of clinical research, the gene-editing treatment has finally treated a rare inherited disorder. Opens gates for ...